Safety and pharmacodynamic effects of a pharmacological chaperone on alpha-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies Journal Articles Refereed uri icon

Overview

Authors

  • Authorship

    • GERMAIN DP
    • SITARAMAN S
    • LOCKHART DJ
    • BOUDES PF
    • GIUGLIANI R
    • HUGHES DA
    • MEHTA A
    • A/PROF Kathleen Nicholls
    • BARISONI L
    • JENNETTE CJ
    • BRAGAT A
    • CASTELLI J

Published in

  • Orphanet Journal of Rare Diseases

Time

Date/time value

  • 2012

Identity

Digital Object Identifier (DOI)

  • 10.1186/1750-1172-7-91

Additional Document Info

Parent Title

  • ORPHANET JOURNAL OF RARE DISEASES

Volume

  • 7

Number

  • ARTN 91

Publisher

  • Biomed Central